A Phase I/II, Non Randomized, Multicenter, Open-Label Study of G1XCGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease

Investigator(s):
Organization: 
UCLA
NCT Number: 
Disease Name: 
X-linked Chronic Granulomatous Disease (X-CGD)
Disease Category: 
Trial Phases: 
Phase 1/2
Trial Status: 
Recruiting
Dr. Caroline Kuo (left) and Dr. Donald Kohn
Dr. Caroline Kuo (left) and Dr. Donald Kohn
Trial Contact: 

Caroline Kuo, M.D. 
(310) 825-6481 
ckuo@mednet.ucla.edu