Efficacy and Safety of Cryopreserved Formulation of Autologous CD34+ Hematopoietic Stem Cells Transduced Ex Vivo With EFS Lentiviral Vector Encoding for Human ADA Gene in Subjects With Severe Combined Immunodeficiency Due to ADA Deficiency
Investigator(s):
Organization:
UCLA
NCT Number:
Disease Name:
Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency (Cryopreserved)
Disease Category:
Trial Phases:
Phase 1/2
Trial Status:
Closed
Trial Contact:
Kit L Shaw, Ph.D.
(310) 825-6188
kshaw@mednet.ucla.edu
