Newsroom

At left, image shows white blood cells (red) from one of the X-CGD clinical trial participants before gene therapy. At right, after gene therapy, white blood cells from the same patient show the presence of the chemicals (blue) needed to attack and destroy bacteria and fungus.
Led by Dr. Donald Kohn and Katelyn Masiuk, the researchers engineered a “viral vector” that would turn on the FoxP3 gene only in regulatory T cells — and not in other types of cells.
Hussein El Kerdi during his 2016 procedure at UCLA. His father, Ali El Kerdi (with cell phone) looks on.
A graphic illustration of a kidney and the message "TO A TRANSPLANT SURGEON, ALL KIDNEYS ARE PINK"
Dr. Jeffrey Veale with (from left) Linda and Eva Maldonado and Vertis Boyce, the recipient of a re-donated kidney.
A photograph of a smiling grandfather and his grandson.
Headshot of Antoni Ribas in a lab coat
Evangelina Vaccaro received Dr. Kohn’s treatment for bubble baby disease in 2012.
Evangelina Vaccaro (far right), who received Dr. Kohn’s treatment for bubble baby disease in 2012, with her family before her first day of school.
A group of surgeons gather around a patient in an operating room. The lights are dimmed and blue-tinged and overhead light blares above.