Media Coverage
"I'm not that person anymore" Live Oak teen's life transformed by rare disease treatment
Icon
Riverbend News
CIRM gets first approval of a one-and-done gene therapy
Icon
Capitol Weekly
FDA approval makes Rocket Pharma gene therapy the first for ultra-rare immune disorder
Icon
Medcity News
They didn't understand why their kids kept getting sick. After a rare diagnosis, a new gene therapy offered hope.
Icon
CBS News
Fat cells burn energy to make heat – making them the next frontier of weight loss therapies
Icon
The Conversation
Rare melanoma trial serves as model for advancing cancer immunotherapy
Icon
Targeted Oncology
Cancer in 2026: How immunotherapy is reshaping the odds
Icon
Cancer Research Institute
Organoid study reveals shared brain pathways across autism-linked variants
Icon
The Transmitter