Media Coverage
They didn't understand why their kids kept getting sick. After a rare diagnosis, a new gene therapy offered hope.
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CBS News
Inhalable gene therapies? Here’s how they could work
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The Medicine Maker
UCLA team developing one-time, inhalable CF gene-editing treatment
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Cystic Fibrosis News Today
Going public: Doudna’s dream team launches groundbreaking sickle cell trial
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Genetic Engineering & Biotechnology News
Health Matters: Bubble boy given new lease on life
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Global News
Atwater girl undergoing innovative treatment
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ABC News
‘Bubble boy’ treatments showing success in spite of funding challenges
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Capitol Weekly
Left in limbo: When pharma halts rare disease research
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Pharmaceutical Technology