Media Coverage
‘Bubble boy’ treatments showing success in spite of funding challenges
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Capitol Weekly
Left in limbo: When pharma halts rare disease research
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Pharmaceutical Technology
Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate
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AP News
Kids with 'bubble boy' disease are dying — even though drug companies have found a cure
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Business Insider
Column: For a man long afflicted with an illness made riskier by COVID-19, hope for the holidays
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Los Angeles Times
California Prop 14 may change lives of sick kids, keep taxpayer funding of stem cell therapy research
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USA Today
The cure factory
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Washington Post