Media Coverage
They didn't understand why their kids kept getting sick. After a rare diagnosis, a new gene therapy offered hope.
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CBS News
Scientists are inventing treatments for devastating diseases. There’s just one problem.
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Washington Post
She was born without an immune system. Gene therapy saved her life.
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The New York Times
Exposure to any germs could've killed her. 11 years later, she's living a normal life thanks to a gene therapy treatment.
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NBC News
They didn't understand why their kids kept getting sick. After a rare diagnosis, a new gene therapy offered hope.
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CBS News
Gene therapy trial helps children with LAD-I
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The Medicine Maker