Media Coverage

A close-up photograph of a researcher with gloved hands holding samples.

AAV vectors in gene therapy: Overcoming barriers for muscular dystrophy treatment

Neurology Live

Oct 28, 2024

Health Matters: Bubble boy given new lease on life

Global News

Aug 27, 2024

Atwater girl undergoing innovative treatment

ABC News

Aug 05, 2024

‘Bubble boy’ treatments showing success in spite of funding challenges

Capitol Weekly

Jul 26, 2024

Left in limbo: When pharma halts rare disease research

Pharmaceutical Technology

Jul 03, 2024

Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate

AP News

Jun 20, 2024

A drug company abandoned a treatment for  ‘bubble boy disease.’ After a 5-year fight, this little girl is about to get it

CNN

Apr 27, 2023

A gene therapy cure for sickle cell is on the horizon

WIRED

Mar 15, 2023

AIDS virus used in gene therapy to fix 'bubble baby’ disease

AP News

May 11, 2021

Column: For a man long afflicted with an illness made riskier by COVID-19, hope for the holidays

Los Angeles Times

Nov 29, 2020