Glossary

An ultraprecise form of gene editing A type of gene therapy that works by delivering genetic material that can directly edit pieces of DNA within a cell. This changes the instructions the DNA encodes for, which ultimately results in an increase or decrease in the production of a certain protein and the restoration of proper cell function. gene editing A type of gene therapy that works by delivering genetic material that can directly edit pieces of DNA within a cell. This changes the instructions the DNA encodes for, which ultimately results in an increase or decrease in the production of a certain protein and the restoration of proper cell function. that enables scientists to correct single-letter mutations in DNA Short for deoxyribonucleic acid, DNA is a double-stranded molecule that serves as the genetic blueprint for living organisms. Composed of four chemical bases, DNA encodes the instructions necessary for protein synthesis and governs the development, function, and inheritance of traits in an organism. DNA Short for deoxyribonucleic acid, DNA is a double-stranded molecule that serves as the genetic blueprint for living organisms. Composed of four chemical bases, DNA encodes the instructions necessary for protein synthesis and governs the development, function, and inheritance of traits in an organism.. Unlike the gene editing platform CRISPR A gene editing technology that enables scientists to remove, add or alter DNA at precise locations in the genome to prevent, treat or cure disease. One component acts as a navigation system that can be programmed to seek out a particular DNA sequence and the other component acts as a pair of "molecular scissors" that can cut two strands of DNA at that location to enable gene modification. CRISPR A gene editing technology that enables scientists to remove, add or alter DNA at precise locations in the genome to prevent, treat or cure disease. One component acts as a navigation system that can be programmed to seek out a particular DNA sequence and the other component acts as a pair of "molecular scissors" that can cut two strands of DNA at that location to enable gene modification., which cuts both strands of the chromosome to make changes to DNA, base editing chemically changes one DNA base letter into another — an A to a G, for example — leaving the chromosome intact.