Autologous Transplantation of Bone Marrow CD34+ Stem/Progenitor Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector for Adenosine Deaminase (ADA)-Deficient Severe Combined Immunodeficiency (SCID)
Investigator(s):
Organization:
UCLA
NCT Number:
Disease Name:
Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency
Disease Category:
Trial Phases:
Phase 1/2
Trial Status:
Closed
Trial Contact:
Kit L. Shaw, Ph.D.
(310) 825-6188
kshaw@mednet.ucla.edu