Autologous Transplantation of Bone Marrow CD34+ Stem/Progenitor Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector for Adenosine Deaminase (ADA)-Deficient Severe Combined Immunodeficiency (SCID)

Investigator(s):
Organization: 
UCLA
NCT Number: 
Disease Name: 
Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency
Disease Category: 
Trial Phases: 
Phase 1/2
Trial Status: 
Closed
Trial Contact: 

Kit L. Shaw, Ph.D. 
(310) 825-6188 
kshaw@mednet.ucla.edu