Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research
Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research
Dantrolene Enhances Antisense-Mediated Exon Skipping in Human and Mouse Models of Duchenne Muscular Dystrophy
Genevieve C. Kendall, Ekaterina I. Mokhonova, Miriana Moran, Natalia E. Sejbuk, Derek W. Wang, Oscar Silva, Richard T. Wang, Leonel Martinez, Qi L. Lu, Robert Damoiseaux, Melissa J. Spencer, Stanley F. Nelson and M. Carrie Miceli